MEDICINE DETAILS
Opfolda
Active ingredient: Miglustat
Neutral reference profile for an independent medicine-access consultancy enquiry about Opfolda (Miglustat). No medicine is offered for sale.
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Choose the strength and pack
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These options are not medical advice, a dosing recommendation, stock confirmation or a sale offer.
ABOUT THIS MEDICINE
What is Opfolda used for?
Opfolda (Miglustat) is a prescription medicine used in combination with cipaglucosidase alfa enzyme replacement therapy for the treatment of adult patients with late-onset Pompe disease.
Pompe disease is an inherited disorder caused by a deficiency of the enzyme acid alpha-glucosidase (GAA), leading to the accumulation of glycogen in muscles. This buildup results in muscle weakness and respiratory problems.
Opfolda binds to cipaglucosidase alfa, stabilizing the enzyme and facilitating its uptake by muscle cells. This combination aids in breaking down glycogen, improving muscle function, and slowing disease progression.
Opfolda is administered orally approximately 1 hour before the cipaglucosidase alfa infusion. Treatment should be initiated and supervised by a doctor experienced in managing Pompe disease or similar disorders.
This information is general and is not medical advice. Talk to your doctor or pharmacist about any treatment decision.
RECORDED PRODUCT PROFILE
Opfolda identity, dosage form and pack information.
The details below are assembled from current catalogue records. They must still be checked against the prescription, medicine box and an official regulatory record.
Recorded strength and pack options
Each row is shown only to help identify the product; it is not stock confirmation or a sale offer.
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65 mg · 4 capsules Catalogue organisation: Amicus Therapeutics GmbH
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65 mg · 24 capsules Catalogue organisation: Amicus Therapeutics GmbH
OFFICIAL SOURCES
Check the Opfolda record at an official source.
Search for “Opfolda” or “Miglustat”. Finding a product in one source does not by itself confirm stock, authorisation in a particular country or suitability for a patient.
OFFICIAL EXTERNAL SOURCE
European Medicines Agency (EMA)
Search medicines evaluated by EMA by brand name or active substance. EMA also links to national registers for nationally authorised products.
↗ OFFICIAL EXTERNAL SOURCE Drugs@FDASearch FDA-approved human drug records by brand name or active ingredient, including current labelling where available.
↗SERVICE BOUNDARY
Information checking and independent enquiry support for Opfolda.
OrphanDrug helps organise the product identity and recorded strength and pack details for an enquiry. It does not sell, take payment for, prescribe, import, dispense or deliver medicines.
Clinical decision: Only a qualified healthcare professional who has assessed the patient can decide whether a product, form or dose is appropriate.
CLEAR ANSWERS
Frequently asked questions about Opfolda
01What is Opfolda?＋
This directory record associates the brand name Opfolda with the active ingredient Miglustat. The brand and ingredient are shown for product identification only, not as treatment or dosing advice.
02Which Opfolda strengths and packs are recorded?＋
The catalogue currently shows: 65 mg · 4 capsules; 65 mg · 24 capsules. Check the complete strength, dosage form and pack description against the prescription and medicine box.
03Who manufactures Opfolda?＋
Catalogue records currently name: Amicus Therapeutics GmbH. This field may identify a manufacturer, marketing-authorisation holder, marketing company or supplier; confirm the exact role on the pack leaflet and official regulatory record.
04Do the listed options confirm stock or access?＋
No. A catalogue record does not confirm current stock, authorisation in a particular country, clinical suitability, import permission or access.
05What affects a possible estimated medicine cost for Opfolda?＋
A possible cost depends on the exact strength, dosage form, pack, quantity, destination and regulatory jurisdiction. Any amount provided after an enquiry is an indicative medicine-cost estimate only, not a selling price for Opfolda, payment request, stock guarantee or binding offer.
06Can I buy Opfolda from this website?＋
No. This website does not sell, take payment for, prescribe, import, dispense or deliver medicines. The form creates an independent consultancy enquiry only.